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Crigler-Najjar syndrome
Crigler-Najjar syndrome
Adeno-associated virus vector serotypes mediate sustained correction of bilirubin UDP glucuronosyltransferase deficiency in rats
Technology / Gene Therapy / Biological Sciences / Molecular / Liver / Animals / Gene transfer techniques / Polymerase Chain Reaction / Adeno-associated virus / Bilirubin / Rats / First Year / Crigler-Najjar syndrome / Rat Model / Molecular Targeted Therapy / Brain Damage / Serotyping / Bile / Animals / Gene transfer techniques / Polymerase Chain Reaction / Adeno-associated virus / Bilirubin / Rats / First Year / Crigler-Najjar syndrome / Rat Model / Molecular Targeted Therapy / Brain Damage / Serotyping / Bile
Adeno-associated virus vector serotypes mediate sustained correction of bilirubin UDP glucuronosyltransferase deficiency in rats
Technology / Gene Therapy / Biological Sciences / Molecular / Liver / Animals / Gene transfer techniques / Polymerase Chain Reaction / Adeno-associated virus / Bilirubin / Rats / First Year / Crigler-Najjar syndrome / Rat Model / Molecular Targeted Therapy / Brain Damage / Serotyping / Bile / Animals / Gene transfer techniques / Polymerase Chain Reaction / Adeno-associated virus / Bilirubin / Rats / First Year / Crigler-Najjar syndrome / Rat Model / Molecular Targeted Therapy / Brain Damage / Serotyping / Bile
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